Oligonucleotide Drugs for Transthyretin Amyloidosis

N Engl J Med. 2018 Nov 22;379(21):2086. doi: 10.1056/NEJMc1810994.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Amyloid Neuropathies, Familial*
  • Amyloidosis*
  • Humans
  • Oligonucleotides
  • Prealbumin

Substances

  • Oligonucleotides
  • Prealbumin

Supplementary concepts

  • Amyloidosis, Hereditary, Transthyretin-Related