Oligonucleotide Drugs for Transthyretin Amyloidosis
N Engl J Med
.
2018 Nov 22;379(21):2086.
doi: 10.1056/NEJMc1810994.
Authors
David Adams
1
,
Philip N Hawkins
2
,
Michael Polydefkis
3
Affiliations
1
Assistance Publique–Hôpitaux de Paris, Le Kremlin-Bicêtre, France david.adams@aphp.fr
2
University College London, London, United Kingdom
3
Johns Hopkins Medicine, Baltimore, MD
PMID:
30484624
DOI:
10.1056/NEJMc1810994
No abstract available
Publication types
Letter
Comment
MeSH terms
Amyloid Neuropathies, Familial*
Amyloidosis*
Humans
Oligonucleotides
Prealbumin
Substances
Oligonucleotides
Prealbumin
Supplementary concepts
Amyloidosis, Hereditary, Transthyretin-Related